Parallel Session 3411
The New Era of Neurometabolic Movement Disorders
Tuesday, October 7, 2025
16:30 - 18:00 | Room TBD
This session is focused on advances in mechanistically-driven targeted precision therapies, that are either in preclinical development, clinical trial or established therapies for children and adults with complex neurometabolic diseases.
Chairs:
Manju Kurian, United Kingdom
Niccolo Mencacci, USA
Presenters:
Precision therapies for NBIAs
Susanne Schneider, Germany
Small Molecule Therapies
Angels Garcia Cazorla, Spain
Genetic Therapies
Toni Pearson, USA
CSPC Liaisons:
Manju Kurian, United Kingdom
Learning Objectives
At the conclusion of this session, participants should be better able to:
- Describe the different precision medicine strategies for treating Neurodegeneration with Brain Iron Accumulation disorders
- Describe the various precision approaches including small molecule therapies for neurometabolic disorders
- Discuss the role of genetic therapy in inherited monogenic neurometabolic disorders, including DNA and RNA therapies
Recommended Audience
Clinician / General Neurology
Fellow / Resident / Student
Health Professional (non-physician)
Industry
Researcher / Basic Science
Education Level
Advanced / Expert
Beginner / Foundational
Intermediate / Experienced
Focus
Translational